Dr Chiara Pizzamiglio Dr Renae Stefanetti Professor Bobby McFarland Dr Naomi Thomas Professor Michael Hanna et al. | Optimizing rare disorder trials: A phase 1a/1b randomized study of KL1333 in adults with mitochondrial disease | 2025 |
|
Dr Chiara Pizzamiglio Dr Rhys Thomas Professor Grainne Gorman Professor Bobby McFarland Professor Michael Hanna et al. | COVID-19-Related Outcomes in Primary Mitochondrial Diseases: An International Study | 2022 |
|