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Browsing publications by Emma Heslop.

Newcastle AuthorsTitleYearFull text
Victoria Hedley
Becca Leary
Dr Anando Sen
Anna Irvin
Emma Heslop
et al.
Performing clinical drug trials in children with a rare disease2024
Emma Heslop
Catherine Turner
Anna Irvin
Professor Volker Straub
Professor Michela Guglieri
et al.
Gene therapy in Duchenne muscular dystrophy: Identifying and preparing for the challenges ahead2021
Ben Porter
Phillip Cammish
Joseph Orrell
Emma Heslop
Dr Chiara Marini Bettolo
et al.
The UK FSHD Patient Registry: A Key Tool in the Facilitation of Clinical Research2019
Ben Porter
Phillip Cammish
Emma Heslop
Dr Chiara Marini Bettolo
The UK Myotonic Dystrophy Patient Registry: A Key Tool in the Facilitation of Clinical Research2019
Emma Heslop
Professor Volker Straub
Emerita Professor Katherine Bushby
The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development2015
Emma Heslop
Professor Volker Straub
Dr Louise Johnston
Emerita Professor Katherine Bushby
The TREAT-NMD Advisory Committee for Therapeutics (TACT): An innovative de-risking model to foster orphan drug development2015
Rachel Thompson
Dr Louise Johnston
Dr Monica Ensini
Emma Heslop
Emerita Professor Katherine Bushby
et al.
RD-Connect: An Integrated Platform Connecting Databases, Registries, Biobanks and Clinical Bioinformatics for Rare Disease Research2014
Dr Pauline McCormack
Emeritus Professor Simon Woods
Emma Heslop
Professor Volker Straub
Emerita Professor Katherine Bushby
et al.
Guidance in social and ethical issues related to clinical, diagnostic care and novel therapies for hereditary neuromuscular rare diseases: "translating" the translational2013
Emma Heslop
Dr Pauline McCormack
Professor Christoph Rehmann-Sutter
Emeritus Professor Simon Woods
The risks of therapeutic misconception and individual patient (n = 1) “trials” in rare diseases such as Duchenne dystrophy2011
Emerita Professor Katherine Bushby
Emma Heslop
Dr Pauline McCormack
Emeritus Professor Simon Woods
The development of antisense oligonucleotide therapies for Duchenne muscular dystrophy: Report on a TREAT-NMD workshop hosted by the European Medicines Agency (EMA), on September 25th 20092010
Emma Heslop
Dr Ali Aldibbiat
Dr Nicola Leech
Professor James Shaw
[abstract] Safety and efficacy of continuous subcutaneous insulin infusion therapy in relation to pre-intervention HbA1c2006